Correcting the mutation at the source
It is incredible to think that today scientists can take cells affected by a disease, manipulate them in the lab, ex-vivo, and return healthy cells to the patient’s body.
At Emendo, we’ve gone a step further to create a safer, more efficient solution that uses an in-vivo strategy, allowing us to treat diseases that until now have been untreatable.
Our engineered CRISPR/Cas9 knows exactly where to cut the DNA to eliminate the mutation and, using a recombination template, significantly increases the accuracy of the insertion of a new DNA sequence. The whole working system is introduced to the patient’s body via injection or inhalation.